Adults with MD in the U.S. report widespread gaps in sexual and reproductive healthcare, according to surveys and interviews ...

A final decision from the FDA is expected by Nov. 27, and if approved, BBP-418 would become the first FDA-approved therapy ...

Dyne launched a global clinical trial, FORZETTO, to test its exon-skipping therapy z-rostudirsen in boys with Duchenne ...

Having a rare disease is not an easy life. I have limb-girdle muscular dystrophy, so in addition to the physical decline of my body, I also need to be hyperaware of my mental health. I don’t think ...

Share this page with email Share this page on Facebook Share this page on X Share this page on Reddit Print Preferred Source on Google This week, I found myself reflecting on how much my life has ...

Share this page with email Share this page on Facebook Share this page on X Share this page on Reddit The “heart-on-a-chip” platform will allow researchers to grow heart cells in a three-dimensional ...

Epicrispr Biotechnologies is partnering with Forge Biologics to support the development of EPI-321, Epicrispr’s one-time epigenetic treatment candidate for facioscapulohumeral muscular dystrophy (FSHD ...

The Committee for Medicinal Products for Human Use (CHMP) has recommended that approval of Agamree (vamorolone) in the European Union be expanded to include people with Duchenne muscular dystrophy ...

Share this page with email Share this page on Facebook Share this page on X Share this page on Reddit Print Preferred Source on Google Last Saturday, I attended “Les Misérables: The Arena Spectacular” ...

A human being since 1972, Patrick Moeschen recently retired after 28 years of teaching music at the middle school level in a public school setting. Diagnosed with Becker muscular dystrophy (MD) in ...

For people with Duchenne muscular dystrophy (DMD), 2026 promises to be a year of tremendous excitement, with several new therapies poised for likely approval in the U.S., according to DMD advocates.