Patients with AQP4-positive NMOSD who converted to seronegativity had a median annualized relapse rate of 0 in a Chinese ...

Patients with ITP treated with thrombopoietin receptor agonists as a second-line therapy had a longer time to next treatment ...

Forgetting to take medication represents the leading driver of suboptimal adherence to long-term prophylaxis in HAE, a study ...

HSCT was linked to higher blood count normalization and failure-free survival rates than symptomatic treatment in patients ...

In a Huntington disease (HD) mouse model, an HSP90 inhibitor reduced mHTT aggregation and improved cognitive function and ...

According to a recent study, treatment trajectories for Wilson disease differ markedly across specialized German centers.

With only 3 HD therapies approved by the FDA, those with the disease are looking to new clinical trials for better answers ...

Missing EEG findings and inconsistent documentation make it difficult for researchers to identify LGS from electronic health ...

Patients with progressive fibrosing interstitial lung diseases, including IPF and PPF, have to wait a long time to receive a ...

A woman with Friedreich ataxia (FA) says living with her rare disease is a balancing act that requires tremendous patience.

Virtual care for MG may alleviate physical and financial burdens, but its drawbacks could affect certain patient groups ...

Rh-null pregnancies can lead to a variety of clinical scenarios, including antenatal alloimmunization, HDFN, and severe fetal ...