The nerve cell-targeting EXG001-307 seems to have a better safety profile than Zolgensma, showing fewer adverse effects on ...

Columnist Helen Baldwin observes SMA Awareness Month by recalling her son's short life with the disease, as well as all she ...

Impressed by the accurate portrayal of emergency rooms on "The Pitt," columnist Sherry Toh hopes to see her own rare disease ...

Columnist Connie Chandler explains how letting go of her "ideal" checklist helped her build a diverse and reliable team of ...

Candis Welch shares her experience with SMA and addresses common misconceptions about disability with clarity, humor, and honesty.

Zolgensma is approved for any type of SMA related to SMN1 mutations, but shouldn't be administered to anyone with an active ...

SMA Awareness Month is a time to shine a light on the everyday challenges and celebrations with this disease, writes ...