Adults with MD in the U.S. report widespread gaps in sexual and reproductive healthcare, according to surveys and interviews ...

A final decision from the FDA is expected by Nov. 27, and if approved, BBP-418 would become the first FDA-approved therapy ...

Dyne launched a global clinical trial, FORZETTO, to test its exon-skipping therapy z-rostudirsen in boys with Duchenne ...

Having a rare disease is not an easy life. I have limb-girdle muscular dystrophy, so in addition to the physical decline of my body, I also need to be hyperaware of my mental health. I don’t think ...

An experimental gene therapy called ATA-200 has shown promising safety and efficacy results in an early clinical trial for children with limb-girdle muscular dystrophy type R5 (LGMDR5). Long-term data ...

Share this page with email Share this page on Facebook Share this page on X Share this page on Reddit Print Preferred Source on Google This week, I found myself reflecting on how much my life has ...

Living with Duchenne muscular dystrophy (DMD) means your loved one will need to adapt to symptom changes over time. Paying close attention to these changes is key because it can help your loved one ...

The Phase 3 portion of a clinical trial testing RGX-202, an investigational gene therapy for Duchenne muscular dystrophy (DMD), met its main goal, the therapy’s developer, Regenxbio, announced in a ...

MDA Engage – Chicago September 25 @ 7:00 PM - September 26 @ 4:45 PM Westin Chicago Lombard 70 Yorktown Shopping Center, Lombard, IL, United States Events Today Next Events Subscribe to calendar ...

Share this page with email Share this page on Facebook Share this page on X Share this page on Reddit Print Preferred Source on Google They say the third time is the charm. However, as a mom to three ...

Bridgebio is providing $100,000 to the Muscular Dystrophy Association (MDA) to advance projects aimed at improving multidisciplinary care for people with limb-girdle muscular dystrophy (LGMD). The ...