Adults with MD in the U.S. report widespread gaps in sexual and reproductive healthcare, according to surveys and interviews ...

A final decision from the FDA is expected by Nov. 27, and if approved, BBP-418 would become the first FDA-approved therapy ...

Dyne launched a global clinical trial, FORZETTO, to test its exon-skipping therapy z-rostudirsen in boys with Duchenne ...

Having a rare disease is not an easy life. I have limb-girdle muscular dystrophy, so in addition to the physical decline of my body, I also need to be hyperaware of my mental health. I don’t think ...

Share this page with email Share this page on Facebook Share this page on X Share this page on Reddit The “heart-on-a-chip” platform will allow researchers to grow heart cells in a three-dimensional ...

Share this page with email Share this page on Facebook Share this page on X Share this page on Reddit Print Preferred Source on Google This week, I found myself reflecting on how much my life has ...

Share this page with email Share this page on Facebook Share this page on X Share this page on Reddit Print Preferred Source on Google They say the third time is the charm. However, as a mom to three ...

On May 1, my daughter Jill graduated from the University of Pittsburgh with a master’s degree in public policy and management. She also received the department’s student achievement award and was the ...

Bridgebio is providing $100,000 to the Muscular Dystrophy Association (MDA) to advance projects aimed at improving multidisciplinary care for people with limb-girdle muscular dystrophy (LGMD). The ...

This article was provided by our partner, the Muscular Dystrophy Association. It has been reviewed by Bionews for accuracy and relevance. The views and opinions expressed are those of the author and ...

An experimental gene therapy called ATA-200 has shown promising safety and efficacy results in an early clinical trial for children with limb-girdle muscular dystrophy type R5 (LGMDR5). Long-term data ...