Binghamton researchers show the drug Vamorolone can treat very young boys with Duchenne muscular dystrophy, preventing muscle loss.

More than 30 rare muscular dystrophy types cause progressive muscle weakness from inherited gene mutations. Combined, they affect about 1 in 5,000 to 8,000 people. Common subtypes vary by age of onset ...

Tracing the impact of a single protein, Piezo1, researchers found that restoring it in muscles affected by Duchenne muscular dystrophy could improve their ability to heal efficiently. One protein, ...

Mutations that lead to muscle atrophy can be repaired with the gene editor CRISPR-Cas9. A team led by ECRC researcher Helena Escobar has now introduced the tool into human muscle stem cells for the ...

Duchenne muscular dystrophy (DMD) is a rare neurological condition that causes severe muscle weakness and intellectual disability. DMD is an inherited (passed down) disorder. The condition is linked ...

Becker muscular dystrophy (BMD) is a type of muscular dystrophy, a genetic condition that weakens and damages muscles. It can worsen with age. However, its symptoms are less severe than those of ...

A Northwestern Medicine study has uncovered how chronic defects in muscle membrane repair can fuel harmful inflammation. The findings offer new details on an essential biological process and may be ...

A research team has discovered that by manipulating a certain protein in the immune system they can slow down disease progression and improve muscle function in Duchenne muscular dystrophy. A team of ...