Columnist G Shellye Horowitz learned the hard way that, as someone with hemophilia, surgical planning ahead of time is ...

Hemophilia is a rare genetic condition that prevents your blood from clotting and can lead to bleeding problems. People with hemophilia can have bleeding episodes that happen without trauma and can ...

Nonfactor therapies may reduce costs associated with bleeding-related hospitalizations and use of bypassing agents. One study ...

WEDNESDAY, April 2, 2025 (HealthDay News) -- The U.S. Food and Drug Administration has approved Qfitlia (fitusiran) for routine prophylaxis to prevent or reduce the frequency of bleeding episodes in ...

People with severe hemophilia A are at risk for prolonged bleeding events that can cause serious complications. To prevent these bleeding events, most people with this condition get injections of a ...

Hemophilia may lead to internal bleeding, particularly in joints and the brain, which could cause pain, swelling, and neurological symptoms. Preventive treatment with clotting factor concentrates and ...

Pfizer’s research partnership with Sangamo Therapeutics produced a hemophilia A gene therapy that reached FDA discussions about a regulatory submission. That’s as far as the alliance will go. Pfizer ...

Shortly after taking reins at BioMarin, CEO Alexander Hardy laid out three paths the company could take for its struggling ...

Amid slow sales, BioMarin will continue to make the gene therapy commercially available in the US, Italy, and Germany while it finalizes next steps.