Discover how prime editing is redefining the future of medicine by offering highly precise, safe, and versatile DNA corrections, bringing hope for more effective treatments for genetic diseases while ...

The Food and Drug Administration’s approval of nearly a dozen gene therapies in the past year, including milestone treatments for sickle cell disease and hemophilia B, has finally ushered in the era ...

For men with hemophilia B, receipt of gene therapy comprising an infusion of etranacogene dezaparvovec results in sustained endogenous factor IX expression and low annualized bleeding rates over five ...

Engineers at the University of Pennsylvania and Rice University have refined a technology for editing individual genetic ...

Sherry Gao, Tyler Daniel (pictured) and their coauthors developed a new tool that can simultaneously and independently edit multiple genes and regulate their expression. Influential inventions often ...

Trailblazing geneticist Pengfei Liu, Ph.D., Associate Professor in the Department of Molecular and Human Genetics at Baylor College of Medicine, is the recipient of the 2026 Edith and Peter O’Donnell ...

The UAE has launched two gene therapy projects targeting the root causes of autism and rare brain disorders, marking a significant shift from symptom management to biological repair. Collaborating ...

Emily Kramer-Golinkoff can’t get enough oxygen with each breath. Advanced cystic fibrosis makes even simple things like walking or showering arduous and exhausting. She has the most common fatal ...

Thanks to advances in imaging and diagnostic technologies, clinicians can now detect many genetic disorders in the womb, ...

This photo provided by Emily’s Entourage in April 2025 shows Emily Kramer-Golinkoff, who has cystic fibrosis caused by a rare genetic mutation, during a trip to Maine. (Emily’s Entourage via AP) Emily ...

Regenerative Medicine Market OverviewThe regenerative medicine market is projected to grow at a robust CAGR of 17% during the forecast period, driven by rising chronic disease incidence, increasing ...